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haemophilia b

Synonyms

Noun

1. hemophilia B

2. haemophilia B, Christmas disease, hemophilia, haemophilia, bleeder's disease

Usage
From Lifelong Injections To One-Time Cure: India Pioneers Lentiviral Gene Therapy for 'Haemophilia A' Patients - ETV Bharat
Fidanacogene Elaparvovec for Hemophilia B — A Multiyear Follow-up Study - The New England Journal of Medicine
Single-Dose Gene Therapy is Potentially Life-Changing for Adults with Hemophilia B - Penn Medicine
Case Report: Severe hemophilia B patient with inhibitor and anaphylaxis reaction to FIX, successfully managed with concizumab prophylaxis therapy - Frontiers
After 4 years, hemophilia B bleeding rates remain low with Hemgenix - Hemophilia News Today
Concizumab prophylaxis in people with haemophilia A or haemophilia B without inhibitors (explorer8): a prospective, multicentre, open-label, randomised, phase 3a trial - The Lancet
NMPA approves BBM and Takeda China’s haemophilia B therapy - Pharmaceutical Technology
UK Approves Marstacimab for Severe Haemophilia A or B - Medscape
Hemgenix shows efficacy among haemophilia B patients - PharmaTimes
Belief, Takeda’s home-grown haemophilia B gene therapy gains nod in China - FirstWord Pharma
rFIXFc Safe and Effective in Treating Hemophilia B - Hematology Advisor
(PDF) Treatment of hemophilia B: focus on recombinant factor IX - ResearchGate
Pfizer Jettisons FDA-Approved Hemophilia B Gene Therapy Beqvez - CGTLive®
Get easily bruised? It may be due to haemophilia B - Healthshots
Marstacimab approved to treat patients aged 12 years and above (weighing at least 35 kg) with haemophilia A or B - GOV.UK
Gene Therapy with Fidanacogene Elaparvovec in Adults with Hemophilia B - The New England Journal of Medicine
First hemophilia B patients in Denmark treated with Hemgenix –... - Hemophilia News Today
Be Bio raises $82m to advance haemophilia B gene therapy to Phase I/II trial - Pharmaceutical Technology
News and Expert Insights in Hemophilia Gene Therapy for Bleeding Disorders Awareness Month 2025 - CGTLive®
Concizumab reduces bleeding in patients without inhibitors - Hemophilia News Today
European Commission Approves Pfizer’s HYMPAVZI™ (marstacimab) for the Treatment of Adults and Adolescents with Severe Hemophilia A or B Without Inhibitors - Business Wire
Pfizer to Discontinue Its Hemophilia B Gene Therapy - MedPage Today
Pfizer discontinues hemophilia treatment Beqvez, emptying its gene therapy portfolio - Fierce Pharma
CSL Behring's Gene Therapy HEMGENIX® (etranacogene dezaparvovec-drlb) Four Years Post-Infusion Data Continue to Show Sustained Efficacy and Safety in Adults with Hemophilia B - PR Newswire
Haemophilia B: My £2.6m blood has 'cured' my haemophilia - BBC
Centessa drops phase 2 hemophilia B drug in wake of Pfizer’s Hympavzi approval - Fierce Biotech
Single-dose gene therapy is potentially life-changing for adults with hemophilia B - Penn Today
Hemophilia B Market Size to Reach USD 24.7 Billion by 2035, Impelled by Advancements in Gene Therapy - BioSpace
CSL Behring announces four-year results for haemophilia B gene therapy Hemgenix - PMLiVE
Pfizer pulls the plug on haemophilia gene therapy - FirstWord Pharma
Pfizer stops commercialization of hemophilia gene therapy Beqvez - Reuters
Be Bio secures $92m to advance BCM treatments - Pharmaceutical Technology
Pfizer receives EU haemophilia B gene therapy approval - European Pharmaceutical Review
Pfizer stops selling hemophilia gene therapy, citing weak demand - BioPharma Dive
$15.7 Bn Haemophilia Treatment Market - Global Industry Trends Opportunities, and Forecasts, 2020-2030 - GlobeNewswire
Pfizer’s bet on gene therapies in haemophilia has been a bust - Pharmaceutical Technology
Gene therapy frees hemophilia patient from constant worry, needles - Harvard Gazette
FDA Approves Pfizer's Hympavzi for Hemophilia A, B - Medscape
CSL Behring treats two patients with gene therapy for haemophilia B - Clinical Trials Arena
ORPHEE: A Real-World Study on rIX-FP Prophylaxis Use in Adolescent/Adult Patients With Hemophilia B - Wiley Online Library
Gene Therapy in Hemophilia: High Hopes and Costs, Low Uptake - Medscape
Children's Hospital of Philadelphia Researchers Find Gene Therapy Shows Long-Term Benefits for Hemophilia B Patients - PR Newswire
Pfizer’s Hympavzi granted MHRA approval to treat haemophilia A and B - PMLiVE
Sanofi’s Qfitlia granted FDA approval to treat haemophilia A or B - PMLiVE
FDA clears Sanofi's siRNA as first rebalancing agent for all haemophilia patients - FirstWord Pharma
U.S. FDA Approves Pfizer’s HYMPAVZI™ (marstacimab-hncq) for the Treatment of Adults and Adolescents with Hemophilia A or B Without Inhibitors - Business Wire
FDA approves Pfizer’s HYMPAVZI to treat haemophilia - Pharmaceutical Technology
Sangamo left solo on haemophilia A gene therapy as Pfizer withdraws support - FirstWord Pharma
Pfizer's haemophilia B gene therapy gets EU green light - pharmaphorum
Sanofi's versatile Qfitlia scores FDA nod to enter crowded hemophilia market - Fierce Pharma
Pfizer quickly expands its hemophilia B gene therapy's reach with EU approval - Fierce Pharma
NICE recommends CSL Behring’s haemophilia B gene therapy Hemgenix - PMLiVE
Germany will reimburse haemophilia gene therapy Hemgenix - pharmaphorum
New Hemophilia Treatment Approved by FDA - Technology Networks
Development of SerpinPC as treatment for hemophilia halted by Centessa - Hemophilia News Today
Value contribution of etranacogene dezaparvovec gene therapy in moderately severe and severe haemophilia B through multi-criteria decision analysis - Wiley Online Library
Pfizer’s Hympavzi receives EC approval to treat haemophilia A and B patients - PMLiVE
ASH 2024 discussions shine spotlight on advances in haemophilia treatments - Pharmaceutical Technology
Hympavzi Recommended for Approval in Europe for Severe Hemophilia A and B - Medscape
Alhemo Once-Daily Treatment for Hemophilia A, B with Inhibitors FDA Approved - Managed Healthcare Executive
EU approves Pfizer's haemophilia therapy Hympavzi - FirstWord Pharma
(fidanacogene elaparvovec), a One-Time Gene Therapy for Adults with Hemophilia B - Business Wire
Pfizer doubles down with its 2nd FDA hemophilia approval in 6 months - Fierce Pharma
uniQure successfully defends haemophilia gene therapy patent against Pfizer - JUVE Patent
CSL Behring’s Hemgenix administered to first haemophilia B patients in Europe - World Pharmaceutical Frontiers
In about-face, hemophilia B therapy Hemgenix to be covered by NHS - Hemophilia News Today
Pfizer rounds out haemophilia portfolio with FDA approval - pharmaphorum
Promoterless Gene Targeting Approach Combined to CRISPR/Cas9 Efficiently Corrects Hemophilia B Phenotype in Neonatal Mice - Frontiers
CRISPR/Cas9 for hemophilia - Hemophilia News Today
Emergent data influences the risk/benefit assessment of hemophilia gene therapy using recombinant adeno-associated virus - Frontiers
Pfizer infringed haemophilia B gene therapy patent - Progress Educational Trust
Figure 2. Identification of the breakpoints from two patients with... - ResearchGate
Consultation publique - FPS Public Health
England, Denmark back CSL’s haemophilia B gene therapy - pharmaphorum
Disease and treatment burden of patients with haemophilia entering the explorer6 non-interventional study - Wiley Online Library
EMA Authorizes Hemophilia B Gene Therapy - Medscape
Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B - The New England Journal of Medicine
Phase 1–2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B - The New England Journal of Medicine
First patients treated with HEMGENIX® (etranacogene dezaparvovec) gene therapy for haemophilia B in Denmark - Mynewsdesk
New gene therapy for hemophilia used for the first time in Austria - MedUni Wien
Haemophilia: Causes and advancements in treatment that you should know - Hindustan Times
Explainer: Why Is Hemophilia B Called Christmas Disease? - Global Biotechnology Company
NHS £2.6m blood infusion transforms life for haemophilia B patients - The Telegraph
FDA approves first gene therapy for Haemophilia B - - European Pharmaceutical Review
Patient perspective on living with mild hemophilia in Germany: results from a nationwide survey - Frontiers
Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial - The Lancet
World Haemophilia Day 2025 — Understanding The Rare Bleeding Disorder - ABP Live English
ABPI cheers new gene therapy for IMF and innovative payment first - Association of the British Pharmaceutical Industry (ABPI)
MHRA grants UK marketing authorisation for Pfizer’s haemophilia treatment - Pf Media
Transformational therapy cures haemophilia B - BBC
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant - The New England Journal of Medicine
CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice - Nature
Haemophilia treatment first to be recommended by NICE as part of new drug pricing agreement - The Pharmaceutical Journal
Therapeutic efficacy in a hemophilia B model using a biosynthetic mRNA liver depot system - Nature
Personal Story: Ashley | Hemophilia - Centers for Disease Control and Prevention | CDC (.gov)
CSL Behring’s Gene Therapy HEMGENIX (etranacogene dezaparvovec): Four Years Post-Infusion Data Continue to Show Sustained Efficacy and Safety in Adults with Haemophilia B - Mynewsdesk
FDA Approves Second Gene Therapy for Hemophilia B - Medscape
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector - Nature
PAM-flexible Cas9-mediated base editing of a hemophilia B mutation in induced pluripotent stem cells - Nature
Case Closed: Famous Royals Suffered From Hemophilia - Science | AAAS
Foreign Language Equivalents
Foreign Language Equivalents of 'haemophilia b'
Language Equivalent   Language Equivalent
French    Spanish
Misspellings - Typos
gaemophilia b,   haemopilia b,   haemophilia n,   ahemophilia b,   heamophilia b,   haemophillia b,   haemopphilia b,   hamophilia b,   haemohilia b,   haeophilia b,   haemoohilia b,   hemophilia b,   haemophili b,   haemopgilia b,   haemophiliaa b,   haemophiloa b,   hsemophilia b,   hawmophilia b,   haempohilia b,   haemphilia b,   haemophiliab ,   haemmophilia b,   haemophi;ia b,   jaemophilia b,   haemo[hilia b,   hameophilia b,   aemophilia b,   haemophlia b,   haemophiliia b,   haeomphilia b,   haeemophilia b,   haemophhilia b,   haemopihlia b,   haemiphilia b,   haemophilis b,   haemophilia bb,   haemopjilia b,   haemophiia b,   haemophiilia b,   haemophila b,   haemophilua b,   haemophilai b,   haemoophilia b,   haemophilia b,   haemophliia b,   haempphilia b,   haemophili ab,   haenophilia b,   haemohpilia b,   haemophiliab,   haemopholia b,   haaemophilia b,   haemophiila b,   haemophikia b,   harmophilia b,   hhaemophilia b,   haemophulia b,   hae,ophilia b,   haemophilia v,   haemophilia
Words Starting with Letter - 'A'
a a battery a billion
a bit a bit much a capella singing
a cappella singing a couple of a few
a fortiori a good deal a great deal
a horizon a hundred a hundred and one
a hundred thousand a hundred times a kempis
a la carte a la mode a level
a little a lot a million
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